Marta, with Niemann Pick C, fights for a cure with gene therapy
Por um escritor misterioso
Descrição
Marta is a four and a half year old girl with Niemann Pick C. This is a rare neurodegenerative genetic disease
mRNA Treatment Rescues Niemann-Pick Disease Type C1 in Patient
Systematic characterization of regulatory variants of blood
Marta – Columbus Children's Foundation
Niemann Pick C Awareness Group
Niemann Pick C Awareness Group
Sialidosis type I fibroblasts respond to treatment with human
News – Page 2 – Columbus Children's Foundation
State of the Science - Beyond Batten Disease Foundation
Traditional Chinese medicine compounds regulate autophagy for
Meet Parker and Woodrow, two AZ children with a rare disease
Frontiers Extremely small and incredibly close: Gut microbes as
Rare performance to fight rare disease
COVID-19: Drug Targets and Potential Treatments
O Portal da Uol publicou - Associação Niemann-Pick Brasil
Selected Abstracts from the 12th Annual Meeting of the Clinical
de
por adulto (o preço varia de acordo com o tamanho do grupo)